Statistical methods in hematology trials
The methods these trials rely on most, based on the statistical analyses posted to ClinicalTrials.gov, with the tutorial that explains each one.
Hazard ratio
Log-rank test
Cochran-Mantel-Haenszel test
Odds ratio
Cox proportional-hazards model
Non-inferiority trial design
ANCOVA
Risk difference
All hematology trials
378 results
- A Study for Patients With Non-Hodgkin’s Lymphomas: Complete Statistical AnalysisIndependent statistical analysis of A Study for Patients With Non-Hodgkin's Lymphomas: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT00542919).
- A Study in Adults With Untreated Acute Lymphoblastic Leukemia: Complete Statistical AnalysisIndependent statistical analysis of A Study in Adults With Untreated Acute Lymphoblastic Leukemia: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT00136435).
- A Study in Participants With Acute Major Bleeding to Evaluate the Ability of Andexanet Alfa to Reverse the Anticoagulation Effect of Direct and Indirect Oral Anticoagulants (Extension Study): Complete Statistical AnalysisIndependent statistical analysis of A Study in Participants With Acute Major Bleeding to Evaluate the Ability of Andexanet Alfa to Reverse the Anticoagulation Effect of Direct and Indirect Oral Anticoagulants (Extension Study):…
- A Study of AG-348 in Adult Participants With Pyruvate Kinase (PK) Deficiency: Complete Statistical AnalysisIndependent statistical analysis of A Study of AG-348 in Adult Participants With Pyruvate Kinase (PK) Deficiency: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov…
- A Study of ASP2215 (Gilteritinib), Administered as Maintenance Therapy Following Induction/Consolidation Therapy for Subjects With FMS-like Tyrosine Kinase 3 (FLT3/ITD) Acute Myeloid Leukemia (AML) in First Complete Remission: Complete Statistical AnalysisIndependent statistical analysis of A Study of ASP2215 (Gilteritinib), Administered as Maintenance Therapy Following Induction/Consolidation Therapy for Subjects With FMS-like Tyrosine Kinase 3 (FLT3/ITD) Acute Myeloid Leukemia (AML) in First Complete Remission:…
- A Study of ASP2215 Versus Salvage Chemotherapy in Patients With Relapsed or Refractory Acute Myeloid Leukemia (AML) With FMS-like Tyrosine Kinase (FLT3) Mutation: Complete Statistical AnalysisIndependent statistical analysis of A Study of ASP2215 Versus Salvage Chemotherapy in Patients With Relapsed or Refractory Acute Myeloid Leukemia (AML) With FMS-like Tyrosine Kinase (FLT3) Mutation: primary endpoint results, effect estimate…
- A Study of BAX 888 in Male Adults With Severe Hemophilia A: Complete Statistical AnalysisIndependent statistical analysis of A Study of BAX 888 in Male Adults With Severe Hemophilia A: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov…
- A Study of BBI608 Administered With Paclitaxel in Adult Patients With Advanced Malignancies: Complete Statistical AnalysisIndependent statistical analysis of A Study of BBI608 Administered With Paclitaxel in Adult Patients With Advanced Malignancies: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on…
- A Study of Bomedemstat (IMG-7289/MK-3543) With and Without ATRA, in Participants With Advanced Myeloid Malignancies (IMG-7289-CTP-101/MK-3543-001): Complete Statistical AnalysisIndependent statistical analysis of A Study of Bomedemstat (IMG-7289/MK-3543) With and Without ATRA, in Participants With Advanced Myeloid Malignancies (IMG-7289-CTP-101/MK-3543-001): primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and…
- A Study of Brentuximab Vedotin in Relapsed or Refractory Non-Hodgkin Lymphoma: Complete Statistical AnalysisIndependent statistical analysis of A Study of Brentuximab Vedotin in Relapsed or Refractory Non-Hodgkin Lymphoma: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results…
- A Study of Decitabine Given Subcutaneously to Adults With Low or Intermediate-1 Risk Myelodysplastic Syndromes (MDS): Complete Statistical AnalysisIndependent statistical analysis of A Study of Decitabine Given Subcutaneously to Adults With Low or Intermediate-1 Risk Myelodysplastic Syndromes (MDS): primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and…
- A Study of DS-1211b in Individuals With PseudoXanthoma Elasticum: Complete Statistical AnalysisIndependent statistical analysis of A Study of DS-1211b in Individuals With PseudoXanthoma Elasticum: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT05569252).
- A Study of E7820 in People With Bone Marrow (Myeloid) Cancers: Complete Statistical AnalysisIndependent statistical analysis of A Study of E7820 in People With Bone Marrow (Myeloid) Cancers: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results…
- A Study of Fitusiran (ALN-AT3SC) in Severe Hemophilia A and B Patients Without Inhibitors: Complete Statistical AnalysisIndependent statistical analysis of A Study of Fitusiran (ALN-AT3SC) in Severe Hemophilia A and B Patients Without Inhibitors: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- A Study of FMT in Patients With AML Allo HSCT in Recipients: Complete Statistical AnalysisIndependent statistical analysis of A Study of FMT in Patients With AML Allo HSCT in Recipients: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov…
- A Study of Galunisertib in Participants With Myelodysplastic Syndromes: Complete Statistical AnalysisIndependent statistical analysis of A Study of Galunisertib in Participants With Myelodysplastic Syndromes: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT02008318).
- A Study of HMPL-306 in Advanced Hematological Malignancies With mIDH: Complete Statistical AnalysisIndependent statistical analysis of A Study of HMPL-306 in Advanced Hematological Malignancies With mIDH: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT04764474).
- A Study Of Inotuzumab Ozogamicin Plus Rituximab For Relapsed/Refractory Aggressive Non-Hodgkin Lymphoma Patients Who Are Not Candidates For Intensive High-Dose Chemotherapy: Complete Statistical AnalysisIndependent statistical analysis of A Study Of Inotuzumab Ozogamicin Plus Rituximab For Relapsed/Refractory Aggressive Non-Hodgkin Lymphoma Patients Who Are Not Candidates For Intensive High-Dose Chemotherapy: primary endpoint results, effect estimate with confidence…
- A Study of Intravenous Mircera in Dialysis Patients With Chronic Renal Disease and Anemia.: Complete Statistical AnalysisIndependent statistical analysis of A Study of Intravenous Mircera in Dialysis Patients With Chronic Renal Disease and Anemia.: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- A Study of Itacitinib (INCB039110) in Combination With Ibrutinib in Subjects With Relapsed or Refractory Diffuse Large B-Cell Lymphoma: Complete Statistical AnalysisIndependent statistical analysis of A Study of Itacitinib (INCB039110) in Combination With Ibrutinib in Subjects With Relapsed or Refractory Diffuse Large B-Cell Lymphoma: primary endpoint results, effect estimate with confidence interval, sample-size…
- A Study of KN046 in Patients With Thymic Carcinoma Who Failed Immune Checkpoint Inhibitors: Complete Statistical AnalysisIndependent statistical analysis of A Study of KN046 in Patients With Thymic Carcinoma Who Failed Immune Checkpoint Inhibitors: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- A Study of LY3039478 in Participants With Advanced Cancer: Complete Statistical AnalysisIndependent statistical analysis of A Study of LY3039478 in Participants With Advanced Cancer: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT01695005).
- A Study of MabThera (Rituximab) in Elderly Patients With Untreated Follicular Non-Hodgkin’s Lymphoma (NHL): Complete Statistical AnalysisIndependent statistical analysis of A Study of MabThera (Rituximab) in Elderly Patients With Untreated Follicular Non-Hodgkin's Lymphoma (NHL): primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- A Study of MabThera/Rituxan (Rituximab) Alone and in Combination With Roferon-A in Patients With Follicular or Other CD20+ Low-Grade (Indolent) Lymphoma: Complete Statistical AnalysisIndependent statistical analysis of A Study of MabThera/Rituxan (Rituximab) Alone and in Combination With Roferon-A in Patients With Follicular or Other CD20+ Low-Grade (Indolent) Lymphoma: primary endpoint results, effect estimate with confidence…
- A Study of Midostaurin Efficacy and Safety in Newly Diagnosed Patients With FLT3-mutated AML: Complete Statistical AnalysisIndependent statistical analysis of A Study of Midostaurin Efficacy and Safety in Newly Diagnosed Patients With FLT3-mutated AML: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- A Study of Mircera (C.E.R.A.) in Patients With Pre-Dialysis Chronic Renal Anemia: Complete Statistical AnalysisIndependent statistical analysis of A Study of Mircera (C.E.R.A.) in Patients With Pre-Dialysis Chronic Renal Anemia: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov…
- A Study of Mircera in Anemic Patients With Chronic Kidney Disease Not Yet on Dialysis.: Complete Statistical AnalysisIndependent statistical analysis of A Study of Mircera in Anemic Patients With Chronic Kidney Disease Not Yet on Dialysis.: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…
- A Study of MK2578 in Patients With Chronic Kidney Disease Who Are Not on Dialysis (2578-002): Complete Statistical AnalysisIndependent statistical analysis of A Study of MK2578 in Patients With Chronic Kidney Disease Who Are Not on Dialysis (2578-002): primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and…
- A Study of Monthly Subcutaneous Mircera for the Treatment of Chronic Renal Anemia in Predialysis Patients Not Treated With ESA.: Complete Statistical AnalysisIndependent statistical analysis of A Study of Monthly Subcutaneous Mircera for the Treatment of Chronic Renal Anemia in Predialysis Patients Not Treated With ESA.: primary endpoint results, effect estimate with confidence interval,…
- A Study of Obinutuzumab + Bendamustine (BG) in Participants With Previously Untreated Chronic Lymphocytic Leukemia (CLL): Complete Statistical AnalysisIndependent statistical analysis of A Study of Obinutuzumab + Bendamustine (BG) in Participants With Previously Untreated Chronic Lymphocytic Leukemia (CLL): primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and…
- A Study of Obinutuzumab in Combination With Idasanutlin and Venetoclax in Participants With Relapsed or Refractory (R/R) Follicular Lymphoma (FL) or Rituximab in Combination With Idasanutlin and Venetoclax in Participants With R/R Diffuse Large B-Cell Lymphoma (DLBCL): Complete Statistical AnalysisIndependent statistical analysis of A Study of Obinutuzumab in Combination With Idasanutlin and Venetoclax in Participants With Relapsed or Refractory (R/R) Follicular Lymphoma (FL) or Rituximab in Combination With Idasanutlin and Venetoclax…
- A Study of ONO-7475 in Patients With Acute Leukemias: Complete Statistical AnalysisIndependent statistical analysis of A Study of ONO-7475 in Patients With Acute Leukemias: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT03176277).
- A Study of Oprozomib, Pomalidomide, and Dexamethasone in Adults With Primary Refractory or Relapsed and Refractory Multiple Myeloma: Complete Statistical AnalysisIndependent statistical analysis of A Study of Oprozomib, Pomalidomide, and Dexamethasone in Adults With Primary Refractory or Relapsed and Refractory Multiple Myeloma: primary endpoint results, effect estimate with confidence interval, sample-size planning…
- A Study of Participant Preference With Subcutaneous Versus Intravenous MabThera/Rituxan in Participants With CD20+ Diffuse Large B-Cell Lymphoma or CD20+ Follicular Non-Hodgkin’s Lymphoma Grades 1, 2 or 3a: Complete Statistical AnalysisIndependent statistical analysis of A Study of Participant Preference With Subcutaneous Versus Intravenous MabThera/Rituxan in Participants With CD20+ Diffuse Large B-Cell Lymphoma or CD20+ Follicular Non-Hodgkin's Lymphoma Grades 1, 2 or 3a:…
- A Study of Patients Who Received Inotuzumab Ozogamicin for B-cell ALL (Acute Lymphoblastic Leukemia) That Occurred Again After the Last Treatment: Complete Statistical AnalysisIndependent statistical analysis of A Study of Patients Who Received Inotuzumab Ozogamicin for B-cell ALL (Acute Lymphoblastic Leukemia) That Occurred Again After the Last Treatment: primary endpoint results, effect estimate with confidence…
- A Study of PCI-32765 (Ibrutinib) Versus Rituximab in Relapsed or Refractory Chronic Leukemia/Lymphoma: Complete Statistical AnalysisIndependent statistical analysis of A Study of PCI-32765 (Ibrutinib) Versus Rituximab in Relapsed or Refractory Chronic Leukemia/Lymphoma: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on…
- A Study of Pembrolizumab (MK-3475) in Relapsed or Refractory Classical Hodgkin’s Lymphoma (rrcHL) or Relapsed or Refractory Primary Mediastinal Large B-cell Lymphoma (rrPMBCL) (MK-3475-B68): Complete Statistical AnalysisIndependent statistical analysis of A Study of Pembrolizumab (MK-3475) in Relapsed or Refractory Classical Hodgkin's Lymphoma (rrcHL) or Relapsed or Refractory Primary Mediastinal Large B-cell Lymphoma (rrPMBCL) (MK-3475-B68): primary endpoint results, effect…
- A Study of Pevonedistat in People With Blood Cancers or Solid Tumors With Kidney or Liver Problems: Complete Statistical AnalysisIndependent statistical analysis of A Study of Pevonedistat in People With Blood Cancers or Solid Tumors With Kidney or Liver Problems: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration,…
- A Study Of PF-04449913 In Japanese Patients With Select Hematologic Malignancies: Complete Statistical AnalysisIndependent statistical analysis of A Study Of PF-04449913 In Japanese Patients With Select Hematologic Malignancies: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results…
- A Study Of PF-04449913 In Select Hematologic Malignancies: Complete Statistical AnalysisIndependent statistical analysis of A Study Of PF-04449913 In Select Hematologic Malignancies: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT00953758).
- A Study Of Pharmacokinetics, Whole Body And Organ Dosimetry, And Biodistribution Of Fission-Derived Iodine I 131 Tositumomab (BEXXAR®) For Patients With Previously Untreated Or Relapsed Follicular Or Transformed Non-Hodgkin’s Lymphoma: Complete Statistical AnalysisIndependent statistical analysis of A Study Of Pharmacokinetics, Whole Body And Organ Dosimetry, And Biodistribution Of Fission-Derived Iodine I 131 Tositumomab (BEXXAR®) For Patients With Previously Untreated Or Relapsed Follicular Or Transformed…
- A Study of Recombinant Von Willebrand Factor (rVWF) in Pediatric and Adult Participants With Severe Von Willebrand Disease (VWD): Complete Statistical AnalysisIndependent statistical analysis of A Study of Recombinant Von Willebrand Factor (rVWF) in Pediatric and Adult Participants With Severe Von Willebrand Disease (VWD): primary endpoint results, effect estimate with confidence interval, sample-size…
- A Study of Rituximab (MabThera) in Participants With Chronic Lymphocytic Leukemia (CLL): Complete Statistical AnalysisIndependent statistical analysis of A Study of Rituximab (MabThera) in Participants With Chronic Lymphocytic Leukemia (CLL): primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov…
- A Study of Subcutaneous (sc) Mircera in Dialysis Patients With Chronic Renal Anemia.: Complete Statistical AnalysisIndependent statistical analysis of A Study of Subcutaneous (sc) Mircera in Dialysis Patients With Chronic Renal Anemia.: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on…
- A Study of the Safety, Tolerability and Effectiveness of EZM0414 (IPN60210) Investigative Product in Participants With Relapsed/Refractory Multiple Myeloma and Relapsed/Refractory Diffuse Large B Cell Lymphoma: Complete Statistical AnalysisIndependent statistical analysis of A Study of the Safety, Tolerability and Effectiveness of EZM0414 (IPN60210) Investigative Product in Participants With Relapsed/Refractory Multiple Myeloma and Relapsed/Refractory Diffuse Large B Cell Lymphoma: primary endpoint…
- A Study to Assess the Efficacy, Safety and Tolerability of IRL201104 in Adults With Active Eosinophilic Esophagitis: Complete Statistical AnalysisIndependent statistical analysis of A Study to Assess the Efficacy, Safety and Tolerability of IRL201104 in Adults With Active Eosinophilic Esophagitis: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration,…
- A Study to Evaluate 3 Dose Schedules of Daratumumab in Participants With Smoldering Multiple Myeloma: Complete Statistical AnalysisIndependent statistical analysis of A Study to Evaluate 3 Dose Schedules of Daratumumab in Participants With Smoldering Multiple Myeloma: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…
- A Study to Evaluate GBT021601-012 Single Dose and Multiple Dose in Participants With Sickle Cell Disease (SCD): Complete Statistical AnalysisIndependent statistical analysis of A Study to Evaluate GBT021601-012 Single Dose and Multiple Dose in Participants With Sickle Cell Disease (SCD): primary endpoint results, effect estimate with confidence interval, sample-size planning illustration,…
- A Study to Evaluate Long-term Safety of CC-486 (Oral Azacitidine) in Subjects With Hematological Disorders: Complete Statistical AnalysisIndependent statistical analysis of A Study to Evaluate Long-term Safety of CC-486 (Oral Azacitidine) in Subjects With Hematological Disorders: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…
- A Study to Evaluate Safety, Efficacy and Pharmacokinetics of Rituximab (MabThera/Rituxan) in Participants With Diffuse Large B Cell Lymphoma (DLBCL) or Follicular Lymphoma (FL): Complete Statistical AnalysisIndependent statistical analysis of A Study to Evaluate Safety, Efficacy and Pharmacokinetics of Rituximab (MabThera/Rituxan) in Participants With Diffuse Large B Cell Lymphoma (DLBCL) or Follicular Lymphoma (FL): primary endpoint results, effect…