Statistical methods in oncology trials
The methods these trials rely on most, based on the statistical analyses posted to ClinicalTrials.gov, with the tutorial that explains each one.
Hazard ratio
Log-rank test
Cochran-Mantel-Haenszel test
Odds ratio
Cox proportional-hazards model
Fisher exact test
Risk difference
Stratified log-rank test
All oncology trials
2,067 results
- Educational Program in Younger Women Who Have Recently Finished Treatment for Stage I or Stage II Breast Cancer: Complete Statistical AnalysisIndependent statistical analysis of Educational Program in Younger Women Who Have Recently Finished Treatment for Stage I or Stage II Breast Cancer: primary endpoint results, effect estimate with confidence interval, sample-size planning…
- Effect of 2-h Infusion of ON 01910.Na in Ovarian Cancer Patients: Complete Statistical AnalysisIndependent statistical analysis of Effect of 2-h Infusion of ON 01910.Na in Ovarian Cancer Patients: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results…
- Effect of Chemotherapy and Radiation Prior to Surgery for Triple Negative Breast Cancer: Complete Statistical AnalysisIndependent statistical analysis of Effect of Chemotherapy and Radiation Prior to Surgery for Triple Negative Breast Cancer: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on…
- Effect of Food Upon Pharmacokinetics of Single Oral Dose of Cediranib (AZD2171, Recentin™): Complete Statistical AnalysisIndependent statistical analysis of Effect of Food Upon Pharmacokinetics of Single Oral Dose of Cediranib (AZD2171, Recentin™): primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on…
- Effect of Increased Circulating Androgens on Granulosa Cell Responses to FSH.: Complete Statistical AnalysisIndependent statistical analysis of Effect of Increased Circulating Androgens on Granulosa Cell Responses to FSH.: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results…
- Effect of Proactive Management of Side Effects on Treatment Compliance in Malignant Melanoma Patients on High-dose Intron A Therapy (Study P04600): Complete Statistical AnalysisIndependent statistical analysis of Effect of Proactive Management of Side Effects on Treatment Compliance in Malignant Melanoma Patients on High-dose Intron A Therapy (Study P04600): primary endpoint results, effect estimate with confidence…
- Effect Of Risedronate On Bone Mass In Older Men Receiving Neoadjuvant Therapy For Prostate Cancer: Complete Statistical AnalysisIndependent statistical analysis of Effect Of Risedronate On Bone Mass In Older Men Receiving Neoadjuvant Therapy For Prostate Cancer: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…
- Effect of Weight Loss on Prostate Cancer Pathology: Complete Statistical AnalysisIndependent statistical analysis of Effect of Weight Loss on Prostate Cancer Pathology: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT00475982).
- Effectiveness and Implementation of mPATH-CRC: Complete Statistical AnalysisIndependent statistical analysis of Effectiveness and Implementation of mPATH-CRC: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT03843957).
- Effects of Itraconazole and Rifampin on the Blood Tazemetostat Levels: Complete Statistical AnalysisIndependent statistical analysis of Effects of Itraconazole and Rifampin on the Blood Tazemetostat Levels: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT04537715).
- Effects of Methylphenidate on Attention Deficits in Childhood Cancer Survivors: Complete Statistical AnalysisIndependent statistical analysis of Effects of Methylphenidate on Attention Deficits in Childhood Cancer Survivors: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT01100658).
- Effects of Muscadine Grape Extract in Men With Prostate Cancer on Androgen Deprivation Therapy: Complete Statistical AnalysisIndependent statistical analysis of Effects of Muscadine Grape Extract in Men With Prostate Cancer on Androgen Deprivation Therapy: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- Effects of Single Agent Niraparib and Niraparib Plus Programmed Cell Death-1 (PD-1) Inhibitors in Non-Small Cell Lung Cancer Participants: Complete Statistical AnalysisIndependent statistical analysis of Effects of Single Agent Niraparib and Niraparib Plus Programmed Cell Death-1 (PD-1) Inhibitors in Non-Small Cell Lung Cancer Participants: primary endpoint results, effect estimate with confidence interval, sample-size…
- Efficacy and Safety of BEZ235 Compared to Everolimus in Patients With Advanced Pancreatic Neuroendocrine Tumors: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of BEZ235 Compared to Everolimus in Patients With Advanced Pancreatic Neuroendocrine Tumors: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…
- Efficacy and Safety of Decitabine as Epigenetic Priming With Induction Chemotherapy in Pediatric Acute Myelogenous Leukemia (AML) Subjects: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Decitabine as Epigenetic Priming With Induction Chemotherapy in Pediatric Acute Myelogenous Leukemia (AML) Subjects: primary endpoint results, effect estimate with confidence interval, sample-size planning…
- Efficacy and Safety of Gadobutrol 1.0 Molar (Gadovist) for Breast MRI: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Gadobutrol 1.0 Molar (Gadovist) for Breast MRI: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results…
- Efficacy and Safety of IGIV-C in Corticosteroid Dependent Patients With Generalized Myasthenia Gravis: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of IGIV-C in Corticosteroid Dependent Patients With Generalized Myasthenia Gravis: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on…
- Efficacy and Safety of LBH589 in Adult Patients With Refractory Chronic Myeloid Leukemia (CML) in Chronic Phase: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of LBH589 in Adult Patients With Refractory Chronic Myeloid Leukemia (CML) in Chronic Phase: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration,…
- Efficacy and Safety of Ofatumumab Retreatment and Maintenance Treatment in Patients With B-cell Chronic Lymphocytic Leukemia (CLL): Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Ofatumumab Retreatment and Maintenance Treatment in Patients With B-cell Chronic Lymphocytic Leukemia (CLL): primary endpoint results, effect estimate with confidence interval, sample-size planning illustration,…
- Efficacy and Safety of Olaparib in Pretreated Patients With Measurable Colorectal Cancer, Stratified by Microsatellite Instability (MSI) Status: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Olaparib in Pretreated Patients With Measurable Colorectal Cancer, Stratified by Microsatellite Instability (MSI) Status: primary endpoint results, effect estimate with confidence interval, sample-size planning…
- Efficacy and Safety of OncoGel™ Added to Chemotherapy and Radiation Before Surgery in Subjects With Esophageal Cancer: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of OncoGel™ Added to Chemotherapy and Radiation Before Surgery in Subjects With Esophageal Cancer: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration,…
- Efficacy and Safety of Pemigatinib in Subjects With Advanced/Metastatic or Surgically Unresectable Cholangiocarcinoma Who Failed Previous Therapy – (FIGHT-202): Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Pemigatinib in Subjects With Advanced/Metastatic or Surgically Unresectable Cholangiocarcinoma Who Failed Previous Therapy - (FIGHT-202): primary endpoint results, effect estimate with confidence interval, sample-size…
- Efficacy and Safety of RAD001 in Treating Plexiform Neurofibromas (PN) Associated With Neurofibromatosis (NF1): Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of RAD001 in Treating Plexiform Neurofibromas (PN) Associated With Neurofibromatosis (NF1): primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- Efficacy and Safety of Simtuzumab (SIM) With FOLFIRI as Second Line Treatment in Colorectal Adenocarcinoma: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Simtuzumab (SIM) With FOLFIRI as Second Line Treatment in Colorectal Adenocarcinoma: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…
- Efficacy and Safety of Simtuzumab in Adults With Primary, Post Polycythemia Vera or Post Essential Thrombocythemia Myelofibrosis: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Simtuzumab in Adults With Primary, Post Polycythemia Vera or Post Essential Thrombocythemia Myelofibrosis: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration,…
- Efficacy and Safety of Tenalisib (RP6530), in Patients With Locally Advanced or Metastatic Breast Cancer: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Tenalisib (RP6530), in Patients With Locally Advanced or Metastatic Breast Cancer: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…
- Efficacy and Safety of Tislelizumab in Combination With Fruquintinib in Participants With Selected Solid Tumors: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Tislelizumab in Combination With Fruquintinib in Participants With Selected Solid Tumors: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…
- Efficacy and Safety Study of CC-4047 (Pomalidomide) to Treat Advanced Soft Tissue Sarcoma: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety Study of CC-4047 (Pomalidomide) to Treat Advanced Soft Tissue Sarcoma: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on…
- Efficacy and Tolerability of ZD6474 in Patients With Thyroid Cancer: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Tolerability of ZD6474 in Patients With Thyroid Cancer: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT00098345).
- Efficacy of Digital Breast Tomosynthesis + Standard 2- Dimensional Mammography in Breast Cancer: Complete Statistical AnalysisIndependent statistical analysis of Efficacy of Digital Breast Tomosynthesis + Standard 2- Dimensional Mammography in Breast Cancer: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on…
- Efficacy of Magnetic Resonance-guided High Intensity Focused Ultrasound for the Ablation of Breast Cancer: Complete Statistical AnalysisIndependent statistical analysis of Efficacy of Magnetic Resonance-guided High Intensity Focused Ultrasound for the Ablation of Breast Cancer: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- Efficacy of Neoadjuvant Chemoradiation for Potentially Resectable Pancreas Cancer: Complete Statistical AnalysisIndependent statistical analysis of Efficacy of Neoadjuvant Chemoradiation for Potentially Resectable Pancreas Cancer: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT00557492).
- Efficacy, Safety and CNS Exposure of G-202 (Mipsagargin) in Patients With Recurrent or Progressive Glioblastoma: Complete Statistical AnalysisIndependent statistical analysis of Efficacy, Safety and CNS Exposure of G-202 (Mipsagargin) in Patients With Recurrent or Progressive Glioblastoma: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…
- Efficacy, Safety and Pharmacokinetics of Oral LDE225 in Treatment of Patients With Nevoid Basal Cell Carcinoma Syndrome (NBCCS): Complete Statistical AnalysisIndependent statistical analysis of Efficacy, Safety and Pharmacokinetics of Oral LDE225 in Treatment of Patients With Nevoid Basal Cell Carcinoma Syndrome (NBCCS): primary endpoint results, effect estimate with confidence interval, sample-size planning…
- Efficacy, Safety, and Pharmacokinetic Profiles of REGN3500 Administered to Adult Patients With Moderate-to-Severe Atopic Dermatitis: Complete Statistical AnalysisIndependent statistical analysis of Efficacy, Safety, and Pharmacokinetic Profiles of REGN3500 Administered to Adult Patients With Moderate-to-Severe Atopic Dermatitis: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…
- EFforT-BCRLIndependent statistical analysis of Effectiveness of Fluoroscopy-guided MLD for Treatment of BCRL: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT02609724).
- Eflornithine and/or Diclofenac in Treating Patients With Sun-Damaged Skin: Complete Statistical AnalysisIndependent statistical analysis of Eflornithine and/or Diclofenac in Treating Patients With Sun-Damaged Skin: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT00601640).
- ELARAAn independent statistical analysis of the phase 2 ELARA trial of tisagenlecleucel in adults with refractory or relapsed follicular lymphoma, covering trial design, the primary complete response endpoint, planned statistical analysis, safety,…
- ELARAIndependent statistical analysis of Efficacy and Safety of Tisagenlecleucel in Adult Patients With Refractory or Relapsed Follicular Lymphoma: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- ELEVATEIndependent statistical analysis of DC Migration Study for Newly-Diagnosed GBM: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT02366728).
- ELPISIndependent statistical analysis of Omission of Surgery in Clinically Low-risk HER2positive Breast Cancer With High HER2 Addiction and a Complete Response Following Standard Anti-HER2-based Neoadjuvant Therapy: primary endpoint results, effect estimate with…
- Eltrombopag Olamine in Treating Thrombocytopenia in Patients With Chronic Myeloid Leukemia or Myelofibrosis Receiving Tyrosine Kinase Therapy: Complete Statistical AnalysisIndependent statistical analysis of Eltrombopag Olamine in Treating Thrombocytopenia in Patients With Chronic Myeloid Leukemia or Myelofibrosis Receiving Tyrosine Kinase Therapy: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration,…
- Embozene Microspheres for Uterine Fibroid Embolization (UFE): Complete Statistical AnalysisIndependent statistical analysis of Embozene Microspheres for Uterine Fibroid Embolization (UFE): primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT01675011).
- EMBRACAIndependent statistical analysis of the EMBRACA phase 3 trial of talazoparib versus physician's choice treatment in advanced and/or metastatic breast cancer patients with BRCA mutation, including progression-free survival, response, overall survival, quality…
- ENABLE IIIAn independent statistical analysis of ENABLE III, a randomized study evaluating early palliative care intervention in patients with advanced cancer and their caregivers.
- Enasidenib in MDS &Non-proliferative Chronic Myelomonocytic Leukemia w/o IDH2 Mutation: Complete Statistical AnalysisIndependent statistical analysis of Enasidenib in MDS &Non-proliferative Chronic Myelomonocytic Leukemia w/o IDH2 Mutation: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT05282459).
- ENB-GS-TBLB for the Diagnosis of PPLs: Complete Statistical AnalysisIndependent statistical analysis of ENB-GS-TBLB for the Diagnosis of PPLs: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT02207478).
- ENDEAVORIndependent statistical analysis of the ENDEAVOR phase 3 trial of carfilzomib and dexamethasone versus bortezomib and dexamethasone in relapsed multiple myeloma, including progression-free survival, overall survival, response, safety, and statistical methodology.
- ENDEAVORIndependent statistical analysis of Phase 3 Study With Carfilzomib and Dexamethasone Versus Bortezomib and Dexamethasone for Relapsed Multiple Myeloma Patients: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and…
- Endobronchial Ultrasound-Guided Transbronchial Needle Aspiration Using a 22 vs 25-Gauge Needle: Complete Statistical AnalysisIndependent statistical analysis of Endobronchial Ultrasound-Guided Transbronchial Needle Aspiration Using a 22 vs 25-Gauge Needle: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results…