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Type 2 Diabetes Phase 3 Cardiovascular Outcomes NCT01394952

REWIND: Complete Statistical Analysis of Dulaglutide in Type 2 Diabetes and Cardiovascular Disease

An independent statistical analysis of the randomized phase 3 REWIND trial comparing dulaglutide with placebo for time-to-event cardiovascular and other clinical outcomes in participants with diabetes mellitus, type 2.

Trial period: 2011-07-22 to 2018-08-21  ·  Phase 3  ·  Enrollment 9901
Scope of this record

This page separates reported trial results from statistical interpretation. The numerical results presented here are restricted to the statistical analyses reported in the ClinicalTrials.gov record.

Registry note: This page provides an independent statistical analysis and educational interpretation of publicly reported results. ClinicalTrials.gov provides the official trial registry record.

1. Trial at a Glance

REWIND was a randomized, double-masked, parallel phase 3 trial comparing dulaglutide with placebo in the therapeutic area of endocrinology, with diabetes mellitus, type 2 and cardiovascular disease listed as conditions.

9901
Enrolled
2 randomized arms
2
Treatment arms
Dulaglutide vs placebo
0.88
Primary CV HR
95.33% CI 0.79–0.99
0.026
Primary P-value
Superiority analysis
FeatureREWIND
Trial nameResearching Cardiovascular Events With a Weekly Incretin in Diabetes (REWIND)
PhasePhase 3
ConditionsCardiovascular Disease; Diabetes Mellitus, Type 2
AllocationRandomized
Design modelParallel
MaskingDouble
Primary purposeTreatment
Enrollment9901
InterventionsDulaglutide; Placebo
Primary endpoint typeTime-to-event
Primary hypothesis typeSuperiority
Lead sponsorEli Lilly and Company
Sponsor typeIndustry
ClinicalTrials.govNCT01394952

2. Clinical Question

The statistical question was whether assignment to dulaglutide, compared with placebo, was associated with a difference in the time to first occurrence of the registered composite cardiovascular outcome: cardiovascular death, non-fatal myocardial infarction, or non-fatal stroke.

Population

Participants enrolled in a phase 3 randomized trial addressing diabetes mellitus, type 2 and cardiovascular disease.

Intervention

Dulaglutide.

Comparator

Placebo.

Primary question

Does dulaglutide change the time to first occurrence of the registered composite cardiovascular outcome relative to placebo?

3. Trial Design

01
Randomize9901 participants
02
AssignDulaglutide or placebo
03
FollowTime-to-event outcomes
04
AnalyzeCox proportional hazards
05
CompareHazard ratios and confidence intervals
ARM A

Dulaglutide

  • Dulaglutide
  • Randomized treatment assignment
  • Time-to-event outcomes evaluated during follow-up
ARM B

Placebo

  • Placebo
  • Randomized treatment assignment
  • Time-to-event outcomes evaluated during follow-up
Allocation
Randomized allocation in a parallel-group design.
Masking
Double masking was recorded in the registry.
Primary purpose
Treatment.
Follow-up
The registered primary endpoint was followed from randomization through first occurrence, death from any cause, or study completion, with a median follow-up of 5.4 years.

4. Endpoints

The registered primary endpoint was a time-to-event composite. The registry also posted seven secondary statistical analyses covering individual cardiovascular components, all-cause mortality, a composite microvascular endpoint, heart-failure events, and hospitalization for unstable angina.

RoleEndpointTime frameAnalysis
Primary Number of participants who experienced an event for time, from randomization to first occurrence of cardiovascular death, non-fatal myocardial infarction, or non-fatal stroke (a composite cardiovascular outcome). From randomization to first occurrence or death from any cause or study completion (Median Follow-Up of 5.4 Years). Cox proportional-hazards model; hazard ratio.
Secondary Time to first occurrence after randomization of cardiovascular death, non-fatal myocardial infarction, or non-fatal stroke, individually. From randomization to first occurrence or study completion (Median Follow-Up of 5.4 Years). Cox proportional-hazards model; hazard ratio.
Secondary Time to all-cause mortality. From randomization to study completion (Median Follow-Up of 5.4 Years). Cox proportional-hazards model; hazard ratio.
Secondary Time to first occurrence after randomization of the composite microvascular endpoint. From randomization to first occurrence or study completion (Median Follow-Up of 5.4 Years). Cox proportional-hazards model; hazard ratio.
Secondary Time to first occurrence after randomization of heart failure requiring hospitalization or an urgent heart failure clinic visit. From randomization to first occurrence or study completion (Median Follow-Up of 5.4 Years). Cox proportional-hazards model; hazard ratio.
Secondary Time to first occurrence after randomization of first hospitalization for unstable angina. From randomization to first occurrence or study completion (Median Follow-Up of 5.4 Years). Cox proportional-hazards model; hazard ratio.

5. Statistical Methodology

Cox proportional-hazards model

The registry identifies a Cox proportional-hazards regression model as the method used for the primary endpoint and all seven posted secondary analyses. The analysis compared placebo with dulaglutide in the all randomized participants population.

Model-based effect measure
HR = estimated hazard in the dulaglutide group ÷ estimated hazard in the placebo group

For this trial, a hazard ratio below 1 indicates a lower estimated instantaneous event rate under dulaglutide than under placebo within the fitted time-to-event model. The hazard ratio is not an absolute risk difference and does not directly state the probability that an individual participant will experience an event.

Analysis population

The statistical analyses were reported for all randomized participants. This is important because the randomized comparison is defined by treatment assignment rather than by whether participants subsequently remain on assigned treatment.

Superiority framework

The primary hypothesis type was superiority. The primary analysis note specifies that superiority was declared if the upper limit of the two-sided 95.33% confidence interval for the hazard ratio was below 1.0, after adjustment for the interim analysis.

Confidence intervals

The primary endpoint used a 95.33% two-sided confidence interval, whereas the posted secondary analyses used 95% two-sided confidence intervals. The different confidence levels are part of the reported statistical framework and should not be silently replaced with a common confidence level.

Multiplicity

The registry notes that, once superiority was achieved for the primary endpoint, multiplicity adjustments using a graphical approach were performed for secondary efficacy endpoints. The secondary analyses were intended to control the overall Type I error rate at a 2-sided alpha level of 0.0467.

Interim analysis

The primary analysis note explicitly states that the superiority criterion was evaluated after adjustment for an interim analysis. The ClinicalTrials.gov record does not provide additional numerical details about the interim boundary, information fraction, or alpha-spending function, so those features are not inferred here.

6. Statistical Methods Explained

Why was a Cox proportional-hazards model used?

The endpoints are times to clinical events rather than simple binary outcomes at a single fixed time. A Cox model is designed for this setting because it uses the ordering and timing of events while allowing participants without an observed event by the end of follow-up to contribute censored follow-up information.

What does the primary HR of 0.88 mean?

An HR of 0.88 means the fitted model estimated a hazard under dulaglutide that was 88% of the corresponding hazard under placebo. Expressed as a relative complement, this corresponds to an estimated 12% lower hazard for the composite event. It does not mean that 12% fewer participants necessarily experienced an event, nor does it mean that every participant had a 12% reduction in personal risk.

Why is the confidence interval important?

The primary 95.33% confidence interval was 0.79 to 0.99. It describes statistical uncertainty around the estimated hazard ratio under the analysis framework. Because the entire interval is below 1.0, the reported estimate is compatible with a hazard reduction relative to placebo under the prespecified superiority criterion. The interval does not describe the range of individual treatment effects across participants.

Why does the p-value not measure effect size?

The primary p-value was 0.026. A p-value addresses the evidence against the relevant null hypothesis under the specified testing framework; it does not quantify how large the treatment effect is. The hazard ratio and its confidence interval describe the estimated relative effect and its precision, while the p-value addresses statistical evidence.

Why does the 95.33% confidence level matter?

The primary endpoint was evaluated with a two-sided 95.33% confidence interval rather than the 95% interval used for the posted secondary analyses. That distinction reflects the trial's reported multiplicity and interim-analysis framework. Replacing the primary interval with a conventional 95% interval would change the stated statistical procedure.

Why does multiplicity matter for the secondary endpoints?

Multiple efficacy endpoints create multiple opportunities for a statistically unusual result to occur by chance. The registry states that a graphical multiplicity adjustment was used for secondary efficacy endpoints to control the overall Type I error rate at a two-sided alpha level of 0.0467. Consequently, secondary p-values should be interpreted within that prespecified multiplicity framework rather than as isolated tests.

7. Primary Result

Composite Cardiovascular Outcome

The primary endpoint measured the time from randomization to first occurrence of cardiovascular death, non-fatal myocardial infarction, or non-fatal stroke. The analysis population was all randomized participants, and the comparison was placebo versus dulaglutide.

Primary hazard ratio

0.88

95.33% two-sided CI: 0.79–0.99   ·   P = 0.026

Analysis: Cox proportional-hazards model  ·  Hypothesis: Superiority

Primary endpoint componentReported analysis
EndpointTime from randomization to first occurrence of cardiovascular death, non-fatal myocardial infarction, or non-fatal stroke
Time frameFrom randomization to first occurrence or death from any cause or study completion (Median Follow-Up of 5.4 Years)
PopulationAll randomized participants
Groups comparedPlacebo vs Dulaglutide
Effect measureHazard ratio
Estimate0.88
Confidence interval95.33% two-sided CI: 0.79–0.99
P-value0.026
Clinical Biostats interpretation

The estimated hazard ratio of 0.88 indicates that the fitted Cox model estimated approximately a 12% lower hazard for the composite cardiovascular outcome with dulaglutide relative to placebo. This is a relative model-based measure over the analyzed follow-up, not a statement that 12% fewer participants experienced an event.

The 0.79–0.99 95.33% confidence interval describes uncertainty around the estimated hazard ratio. Its upper limit is below 1.0, which is the criterion specified in the registry analysis note for declaring superiority after adjustment for the interim analysis.

The p-value of 0.026 describes statistical evidence under the specified hypothesis-testing framework; it does not measure the magnitude or clinical importance of the treatment effect. The magnitude is described by the hazard ratio, while the confidence interval provides information about its precision.

As with any Cox-model hazard ratio, interpretation depends on the model and its proportional-hazards framework. The ClinicalTrials.gov record does not report a diagnostic assessment of that assumption, so no independent conclusion about proportionality is made here.

8. Secondary Endpoint Results

The registry contains seven posted secondary statistical analyses. Each used a Cox proportional-hazards model in all randomized participants, comparing placebo with dulaglutide. The secondary analyses used two-sided 95% confidence intervals and were subject to the reported graphical multiplicity adjustment.

Secondary endpointHR95% CIP-valueAnalysis note
Cardiovascular death 0.91 0.78–1.06 0.211 Death from CV causes
Non-fatal myocardial infarction 0.96 0.79–1.16 0.652 Nonfatal MI
Non-fatal stroke 0.76 0.61–0.95 0.017 Nonfatal stroke
All-cause mortality 0.90 0.80–1.01 0.067 Time to all cause mortality
Composite microvascular endpoint 0.86 0.79–0.93 <0.001 Microvascular endpoint
Heart failure requiring hospitalization or an urgent heart failure clinic visit 0.93 0.77–1.12 0.456 Heart failure event
First hospitalization for unstable angina 1.14 0.84–1.54 0.413 Hospitalization for unstable angina

Cardiovascular Death

Hazard ratio

0.91

95% two-sided CI: 0.78–1.06   ·   P = 0.211

The estimated hazard ratio was below 1, but the confidence interval included 1.0. The reported p-value was 0.211. Within the stated superiority framework, this result does not provide the same statistical evidence as the primary composite analysis.

Non-fatal Myocardial Infarction

Hazard ratio

0.96

95% two-sided CI: 0.79–1.16   ·   P = 0.652

The estimated hazard ratio was close to 1, with a confidence interval extending on both sides of 1.0. The p-value was 0.652. This component therefore provides a different statistical pattern from the overall composite endpoint.

Non-fatal Stroke

Hazard ratio

0.76

95% two-sided CI: 0.61–0.95   ·   P = 0.017

The estimated hazard ratio of 0.76 corresponds to an estimated 24% lower hazard for non-fatal stroke with dulaglutide relative to placebo. The confidence interval remained below 1.0, while the reported p-value was 0.017. Because this was a secondary endpoint, its interpretation belongs within the trial's stated graphical multiplicity procedure.

All-cause Mortality

Hazard ratio

0.90

95% two-sided CI: 0.80–1.01   ·   P = 0.067

The estimated hazard ratio indicates a lower estimated hazard under dulaglutide, but the 95% confidence interval extended slightly above 1.0. The reported p-value was 0.067. The hazard ratio should therefore be distinguished from the binary question of whether a conventional significance threshold has been crossed.

Composite Microvascular Endpoint

Hazard ratio

0.86

95% two-sided CI: 0.79–0.93   ·   P < 0.001

The estimated hazard ratio corresponds to an estimated 14% lower hazard for the composite microvascular endpoint with dulaglutide relative to placebo. The confidence interval remained below 1.0 and the reported p-value was <0.001. As a secondary endpoint, this result remains subject to the stated multiplicity framework.

Heart Failure Requiring Hospitalization or an Urgent Heart Failure Clinic Visit

Hazard ratio

0.93

95% two-sided CI: 0.77–1.12   ·   P = 0.456

The estimated hazard ratio was 0.93, with a confidence interval extending from 0.77 to 1.12. The p-value was 0.456. The interval therefore includes both a potentially lower and a potentially higher hazard relative to placebo under the fitted model.

First Hospitalization for Unstable Angina

Hazard ratio

1.14

95% two-sided CI: 0.84–1.54   ·   P = 0.413

The estimated hazard ratio of 1.14 is above 1, corresponding to a higher estimated hazard under dulaglutide relative to placebo in the fitted model. The confidence interval includes 1.0 and is relatively broad, extending from 0.84 to 1.54. The p-value was 0.413.

9. Reading the Secondary Results as a Statistical Set

The seven secondary analyses illustrate why a clinical trial should not be reduced to a list of isolated p-values. The effect estimates range from 0.76 for non-fatal stroke to 1.14 for first hospitalization for unstable angina, and the corresponding confidence intervals differ substantially in width.

Statistical featureWhat the REWIND results illustrate
Relative effectHazard ratios below 1 indicate lower estimated hazards; a hazard ratio above 1 indicates a higher estimated hazard.
PrecisionConfidence-interval width varies across endpoints, reflecting different amounts of statistical information.
Null valueFor a hazard ratio, 1.0 is the relevant no-difference value.
MultiplicitySecondary efficacy endpoints were subject to the reported graphical adjustment controlling the overall Type I error rate at a two-sided alpha level of 0.0467.
Endpoint compositionA composite endpoint and its individual components can produce different estimates because they measure different event processes.
Do not overinterpret component results: the primary composite endpoint combines cardiovascular death, non-fatal myocardial infarction, and non-fatal stroke. Its hazard ratio cannot be assumed to equal the hazard ratio of any one component. The individual component analyses are separate time-to-event analyses and should be interpreted on their own statistical definitions.

10. Safety Results

The ClinicalTrials.gov record reports serious adverse events by treatment arm as affected participants divided by participants at risk.

Safety measurePlaceboDulaglutide
Serious adverse events2044/49491991/4943

These figures report the number affected and the corresponding number at risk in each arm. They are not presented here as a formal comparative safety effect measure because the statistical analyses posted on ClinicalTrials.gov do not report a hazard ratio, confidence interval, or p-value for serious adverse events.

Placebo

2044/4949 participants experienced serious adverse events among the reported participants at risk.

Dulaglutide

1991/4943 participants experienced serious adverse events among the reported participants at risk.

11. Primary Endpoint: What the Hazard Ratio Does — and Does Not — Mean

Relative effect

The primary HR of 0.88 means the fitted Cox model estimated the hazard for the composite cardiovascular outcome under dulaglutide to be 88% of the hazard under placebo. This is equivalent to an estimated 12% lower hazard in relative terms.

It does not mean that 12% of participants avoided an event, that 12% fewer participants necessarily experienced the event, or that every individual participant had exactly a 12% reduction in risk.

Confidence interval

The primary 95.33% confidence interval was 0.79–0.99. This quantifies uncertainty around the estimated hazard ratio within the reported statistical framework. It is not a prediction interval for individual participants and does not describe the distribution of treatment effects across people.

P-value

The primary p-value was 0.026. The p-value measures evidence against the relevant null hypothesis under the specified testing procedure. It is not a measure of effect size, clinical importance, or the probability that the null hypothesis is true.

Censoring and follow-up

The primary endpoint was followed from randomization until first occurrence, death from any cause, or study completion, with a median follow-up of 5.4 years. Time-to-event methods allow participants with incomplete event observation to contribute their available follow-up rather than requiring every participant to have an observed event.

12. Multiplicity and Interim Analysis

The primary analysis contains two important pieces of statistical design information. First, superiority was declared if the upper limit of the two-sided 95.33% confidence interval was below 1.0, after adjustment for the interim analysis. Second, once superiority was achieved for the primary endpoint, multiplicity adjustments using a graphical approach were performed for secondary efficacy endpoints.

Interim analysis

The primary analysis note explicitly accounts for an interim analysis. This means the primary confidence interval and superiority criterion should be interpreted within a design that anticipated examination of accumulating information.

Secondary multiplicity

The registry states that secondary efficacy endpoints were adjusted using a graphical approach to control the overall Type I error rate at a two-sided alpha level of 0.0467.

These features matter because an unadjusted interpretation of every individual p-value would ignore the trial's prespecified testing structure. The reported primary endpoint and secondary endpoints do not all occupy the same statistical role.

13. Analysis Population and Randomization

The primary and secondary analyses were reported using all randomized participants. This is consistent with the intention-to-treat principle: the treatment comparison is anchored to randomized assignment rather than being redefined according to treatment actually received after randomization.

Why randomization matters
Randomization → comparable treatment assignment framework → between-group outcome comparison

Randomization establishes the treatment-assignment mechanism. The subsequent statistical model estimates how event times differed between those randomized groups. It does not require that every participant remain continuously exposed to the assigned intervention for the randomized comparison to retain its intended meaning.

The ClinicalTrials.gov record identifies the allocation as randomized and the design model as parallel. They do not provide additional randomization-stratification variables, so no stratification factors are introduced here.

14. Trial Timeline

2011-07-22

Trial start

The REWIND trial began on July 22, 2011.

Phase 3

Randomized cardiovascular-outcome evaluation

The study used a randomized, double-masked, parallel design comparing dulaglutide with placebo.

2018-08-21

Primary completion

The registry lists August 21, 2018 as the primary completion date.

Completed

Results posted

The ClinicalTrials.gov record is marked completed and reports six posted outcome measures and eight posted statistical analyses.

15. What the Primary Result Says Statistically

The primary analysis combines several pieces of information that should be read together rather than separately. The hazard ratio of 0.88 gives the relative effect estimate. The 0.79–0.99 confidence interval describes uncertainty around that estimate. The 0.026 p-value describes the evidence against the relevant null hypothesis under the specified testing framework.

QuantityREWIND primary resultStatistical role
Hazard ratio0.88Estimated relative treatment effect
95.33% CI0.79–0.99Uncertainty around the hazard-ratio estimate
P-value0.026Evidence against the null under the specified testing procedure
HypothesisSuperiorityTests whether the treatment effect is consistent with a hazard ratio below 1
AnalysisCox proportional-hazards modelModel used to estimate the hazard ratio
PopulationAll randomized participantsPreserves the randomized treatment-assignment comparison

16. Limitations

17. Why This Trial Matters Statistically

REWIND is a useful teaching case because the registry-reported statistical record brings together the core elements of modern time-to-event analysis: randomization, masking, a composite cardiovascular endpoint, Cox regression, hazard ratios, confidence intervals, superiority testing, an interim analysis, and multiplicity adjustment across secondary efficacy endpoints.

ConceptHow it appears in REWIND
RandomizationThe trial used randomized allocation in a parallel-group design.
BlindingThe registry records double masking.
Time-to-event endpointThe primary outcome measures time from randomization to first occurrence of a cardiovascular event in a composite endpoint.
Cox modelThe primary and posted secondary analyses used Cox proportional-hazards regression.
Hazard ratioHR was the reported effect measure for the time-to-event analyses.
Confidence intervalThe primary analysis used a two-sided 95.33% CI; secondary analyses used two-sided 95% CIs.
SuperiorityThe primary hypothesis type was superiority.
Interim analysisThe primary superiority criterion was adjusted for an interim analysis.
MultiplicityA graphical approach was used for secondary efficacy endpoints, with the stated overall two-sided alpha level of 0.0467.
Composite endpointCardiovascular death, non-fatal myocardial infarction, and non-fatal stroke formed the primary composite outcome.
Component analysisThe three individual cardiovascular components were also analyzed as secondary time-to-event outcomes.

18. Statistical Concepts in This Trial

Learn more about the methods used in this trial:

19. Related Statistical Calculators

20. Sources

Continue through the Clinical Biostats statistical library

Use the related tutorials and calculators to explore the survival-analysis concepts illustrated by the REWIND statistical record.

21. Record Summary

REWIND provides a clear example of a randomized phase 3 time-to-event analysis. The primary endpoint was a composite of cardiovascular death, non-fatal myocardial infarction, and non-fatal stroke, analyzed in all randomized participants using a Cox proportional-hazards model. The reported hazard ratio was 0.88, with a two-sided 95.33% confidence interval of 0.79–0.99 and a p-value of 0.026. The registry identifies the hypothesis as superiority and specifies that the upper confidence-limit criterion was evaluated after adjustment for an interim analysis. Secondary efficacy endpoints were analyzed with the same Cox-model framework and were subject to a graphical multiplicity adjustment controlling the overall Type I error rate at a two-sided alpha level of 0.0467.

The statistical lesson is broader than the primary p-value. A time-to-event trial should be interpreted through the combination of randomized treatment assignment, endpoint definition, hazard ratio, confidence interval, p-value, analysis population, and multiplicity and interim-analysis rules. The secondary endpoint results further demonstrate why individual components of a composite outcome can have different effect estimates and different levels of statistical precision.

Clinical Biostats methodology: A trial-results page should not merely repeat a registry record. The goal is to reconstruct the statistical story of the trial while clearly separating reported evidence from educational interpretation and avoiding conclusions that are not supported by the ClinicalTrials.gov record.