Statistical methods in endocrinology & metabolism trials
The methods these trials rely on most, based on the statistical analyses posted to ClinicalTrials.gov, with the tutorial that explains each one.
ANCOVA
Multiple imputation / missing data
Non-inferiority trial design
Logistic regression
Odds ratio
Mixed-effects model
MMRM (mixed model for repeated measures)
Cochran-Mantel-Haenszel test
All endocrinology & metabolism trials
1,009 results
- Effects of Once and Twice Daily Dosing Regimen of Ertugliflozin (PF-04971729, MK-8835) In Participants With Type 2 Diabetes (MK-8835-040): Complete Statistical AnalysisIndependent statistical analysis of Effects of Once and Twice Daily Dosing Regimen of Ertugliflozin (PF-04971729, MK-8835) In Participants With Type 2 Diabetes (MK-8835-040): primary endpoint results, effect estimate with confidence interval, sample-size…
- Effects of Pioglitazone on High-density Lipoprotein (HDL) Function in Persons With Diabetes: Complete Statistical AnalysisIndependent statistical analysis of Effects of Pioglitazone on High-density Lipoprotein (HDL) Function in Persons With Diabetes: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov…
- Effects of Roflumilast on Insulin and Blood Sugar Levels in Prediabetic Overweight and Obese Individuals: Complete Statistical AnalysisIndependent statistical analysis of Effects of Roflumilast on Insulin and Blood Sugar Levels in Prediabetic Overweight and Obese Individuals: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…
- Effects of Rosiglitazone on Renal Hemodynamics and Proteinuria of Type 2 Diabetic Patients With Renal Insufficiency Due to Overt Diabetic Nephropathy: Complete Statistical AnalysisIndependent statistical analysis of Effects of Rosiglitazone on Renal Hemodynamics and Proteinuria of Type 2 Diabetic Patients With Renal Insufficiency Due to Overt Diabetic Nephropathy: primary endpoint results, effect estimate with confidence…
- Effects of Rosiglitazone on the Metabolic Phenotype of Impaired Glucose Tolerance in Youth: Complete Statistical AnalysisIndependent statistical analysis of Effects of Rosiglitazone on the Metabolic Phenotype of Impaired Glucose Tolerance in Youth: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on…
- Effects of Sitagliptin on Postprandial Lipemia in Men With Type 2 Diabetes: Complete Statistical AnalysisIndependent statistical analysis of Effects of Sitagliptin on Postprandial Lipemia in Men With Type 2 Diabetes: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov…
- Efficacy & Safety of Inhaled Insulin in Type 1 Diabetes: Complete Statistical AnalysisIndependent statistical analysis of Efficacy & Safety of Inhaled Insulin in Type 1 Diabetes: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT00308308).
- Efficacy and Safety of 3 Doses of BI1356 (Linagliptin) in Type 2 Diabetes Patients: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of 3 Doses of BI1356 (Linagliptin) in Type 2 Diabetes Patients: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- Efficacy and Safety of Alogliptin Used in Combination With Sulfonylurea in Participants With Type 2 Diabetes in Japan: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Alogliptin Used in Combination With Sulfonylurea in Participants With Type 2 Diabetes in Japan: primary endpoint results, effect estimate with confidence interval, sample-size planning…
- Efficacy and Safety of B I1356 (Linagliptin) vs. Placebo Added to Metformin Background Therapy in Patients With Type 2 Diabetes: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of B I1356 (Linagliptin) vs. Placebo Added to Metformin Background Therapy in Patients With Type 2 Diabetes: primary endpoint results, effect estimate with confidence interval,…
- Efficacy and Safety of BI 10773 in Combination With Insulin in Patients With Type 2 Diabetes: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of BI 10773 in Combination With Insulin in Patients With Type 2 Diabetes: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and…
- Efficacy and Safety of Dapagliflozin in Combination With Metformin in Type 2 Diabetes Patients: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Dapagliflozin in Combination With Metformin in Type 2 Diabetes Patients: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- Efficacy and Safety of Empagliflozin (BI 10773) in Patients With Type 2 Diabetes and Renal Impairment: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Empagliflozin (BI 10773) in Patients With Type 2 Diabetes and Renal Impairment: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and…
- Efficacy and Safety of Empagliflozin (BI 10773) Versus Placebo and Sitagliptin Over 24 Weeks in Patients With Type 2 Diabetes: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Empagliflozin (BI 10773) Versus Placebo and Sitagliptin Over 24 Weeks in Patients With Type 2 Diabetes: primary endpoint results, effect estimate with confidence interval,…
- Efficacy and Safety of Exenatide in Japanese Patients With Type 2 Diabetes Who Are Treated With Oral Antidiabetic(s): Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Exenatide in Japanese Patients With Type 2 Diabetes Who Are Treated With Oral Antidiabetic(s): primary endpoint results, effect estimate with confidence interval, sample-size planning…
- Efficacy and Safety of MP-513 in Combination With Metformin in Patients With Type 2 Diabetes: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of MP-513 in Combination With Metformin in Patients With Type 2 Diabetes: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…
- Efficacy and Safety of Sitagliptin/Metformin Fixed-Dose Combination (FDC) Compared to Glimepiride in Participants With Type 2 Diabetes Mellitus (MK-0431A-202): Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Sitagliptin/Metformin Fixed-Dose Combination (FDC) Compared to Glimepiride in Participants With Type 2 Diabetes Mellitus (MK-0431A-202): primary endpoint results, effect estimate with confidence interval, sample-size…
- Efficacy and Safety of Sotagliflozin Versus Placebo in Patients With Type 2 Diabetes Mellitus Not Currently Treated With Antidiabetic Therapy: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Sotagliflozin Versus Placebo in Patients With Type 2 Diabetes Mellitus Not Currently Treated With Antidiabetic Therapy: primary endpoint results, effect estimate with confidence interval,…
- Efficacy and Safety of Teneligliptin in Chinese Patients With Type 2 Diabetes Mellitus: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety of Teneligliptin in Chinese Patients With Type 2 Diabetes Mellitus: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on…
- Efficacy and Safety Study of Saxagliptin + Metformin Immediate Release (IR) Versus Metformin IR Alone in Type 2 Diabetes Mellitus: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety Study of Saxagliptin + Metformin Immediate Release (IR) Versus Metformin IR Alone in Type 2 Diabetes Mellitus: primary endpoint results, effect estimate with confidence interval,…
- Efficacy and Safety Study of TA-7284 in Patients With Type 2 Diabetes: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety Study of TA-7284 in Patients With Type 2 Diabetes: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov…
- Efficacy and Safety Study of Velaglucerase Alfa in Children and Adolescents With Type 3 Gaucher Disease: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety Study of Velaglucerase Alfa in Children and Adolescents With Type 3 Gaucher Disease: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and…
- Efficacy and Safety Study of WTX101 (ALXN1840) in Adult Wilson Disease Patients: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety Study of WTX101 (ALXN1840) in Adult Wilson Disease Patients: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov…
- Efficacy and Safety Study With Empagliflozin (BI 10773) vs. Placebo as add-on to Metformin or Metformin Plus Sulfonylurea Over 24 Weeks in Patients With Type 2 Diabetes: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety Study With Empagliflozin (BI 10773) vs. Placebo as add-on to Metformin or Metformin Plus Sulfonylurea Over 24 Weeks in Patients With Type 2 Diabetes: primary…
- Efficacy and Safety Trial to Evaluate the Effect of SCH 497079 on Weight in Obese and Overweight Participants (Study P05483)(COMPLETED): Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety Trial to Evaluate the Effect of SCH 497079 on Weight in Obese and Overweight Participants (Study P05483)(COMPLETED): primary endpoint results, effect estimate with confidence interval,…
- Efficacy and Safety, Long-term Study of Zinc Acetate to Treat Wilson’s Disease in Japan.: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Safety, Long-term Study of Zinc Acetate to Treat Wilson's Disease in Japan.: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- Efficacy and Tolerability of an Intra-Nasal Testosterone Product: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Tolerability of an Intra-Nasal Testosterone Product: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT00975650).
- Efficacy and Tolerability of ZD6474 in Patients With Thyroid Cancer: Complete Statistical AnalysisIndependent statistical analysis of Efficacy and Tolerability of ZD6474 in Patients With Thyroid Cancer: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT00098345).
- Efficacy of Aliskiren in the Treatment of Diabetic Macular Edema: Complete Statistical AnalysisIndependent statistical analysis of Efficacy of Aliskiren in the Treatment of Diabetic Macular Edema: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT00768040).
- Efficacy of Corifollitropin Alfa in Obese Women in Terms of Clinical and Molecular Parameters of IVF Success: Complete Statistical AnalysisIndependent statistical analysis of Efficacy of Corifollitropin Alfa in Obese Women in Terms of Clinical and Molecular Parameters of IVF Success: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration,…
- Efficacy of Intralesional Sodium Thiosulfate Versus Intralesional Saline for Dystrophic and Idiopathic Calcinosis Cutis: Complete Statistical AnalysisIndependent statistical analysis of Efficacy of Intralesional Sodium Thiosulfate Versus Intralesional Saline for Dystrophic and Idiopathic Calcinosis Cutis: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- Efficacy of Laser Debridement on Pain and Bacterial Load in Chronic Wounds: Complete Statistical AnalysisIndependent statistical analysis of Efficacy of Laser Debridement on Pain and Bacterial Load in Chronic Wounds: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov…
- Efficacy of Neoadjuvant Chemoradiation for Potentially Resectable Pancreas Cancer: Complete Statistical AnalysisIndependent statistical analysis of Efficacy of Neoadjuvant Chemoradiation for Potentially Resectable Pancreas Cancer: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT00557492).
- Efficacy of Once-Weekly Exenatide Versus Once or Twice Daily Insulin Detemir in Patients With Type 2 Diabetes: Complete Statistical AnalysisIndependent statistical analysis of Efficacy of Once-Weekly Exenatide Versus Once or Twice Daily Insulin Detemir in Patients With Type 2 Diabetes: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration,…
- Efficacy Of Quadratus Lumborum II Block For Laparoscopic Sleeve Gastrectomy: Complete Statistical AnalysisIndependent statistical analysis of Efficacy Of Quadratus Lumborum II Block For Laparoscopic Sleeve Gastrectomy: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT04073056).
- Efficacy vs Placebo as Initial Combination Therapy With Pioglitazone: Complete Statistical AnalysisIndependent statistical analysis of Efficacy vs Placebo as Initial Combination Therapy With Pioglitazone: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT00641043).
- EFFORTIndependent statistical analysis of Effect of Pioglitazone on Insulin Resistance, Atherosclerosis Progression and Clinical Course of Coronary Heart Disease: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…
- EHR-WWCIndependent statistical analysis of EHR Embedded Comparative Effectiveness Studies--WWC: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT04514679).
- Eltrombopag for Fanconi Anemia: Complete Statistical AnalysisIndependent statistical analysis of Eltrombopag for Fanconi Anemia: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT03206086).
- Empagliflozin (BI 10773) Dose Finder Study in Japanese Patients With Type 2 Diabetes Mellitus: Complete Statistical AnalysisIndependent statistical analysis of Empagliflozin (BI 10773) Dose Finder Study in Japanese Patients With Type 2 Diabetes Mellitus: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- Empagliflozin as Adjunctive to Insulin Therapy Over 26 Weeks in Patients With T1DM (EASE-3): Complete Statistical AnalysisIndependent statistical analysis of Empagliflozin as Adjunctive to Insulin Therapy Over 26 Weeks in Patients With T1DM (EASE-3): primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based…
- EMPOWER-MomIndependent statistical analysis of Postpartum Weight Loss for Women at Elevated Cardiovascular Risk: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT04914819).
- EMPOWER-T2DIndependent statistical analysis of EMI-EHP Weight Management and Type 2 Diabetes Pragmatic Trial: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT04531176).
- ENCOREIndependent statistical analysis of A Study of Eliglustat Tartrate (Genz-112638) in Patients With Gaucher Disease Who Have Reached Therapeutic Goals With Enzyme Replacement Therapy (ENCORE): primary endpoint results, effect estimate with confidence…
- EndoTAG-1+GEM vs GEM in Patients With Locally Advanced/Metastatic Pancreatic Adenocarcinoma Failed on FOLFIRINOX: Complete Statistical AnalysisIndependent statistical analysis of EndoTAG-1+GEM vs GEM in Patients With Locally Advanced/Metastatic Pancreatic Adenocarcinoma Failed on FOLFIRINOX: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on…
- Endothelial Hyperpolarization in Humans: Complete Statistical AnalysisIndependent statistical analysis of Endothelial Hyperpolarization in Humans: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on ClinicalTrials.gov results (NCT00166166).
- ENERGIZEIndependent statistical analysis of A Study to Evaluate a Potassium Normalization Treatment Regimen Including Sodium Zirconium Cyclosilicate (ZS) Among Patients With S-K ≥5.8: primary endpoint results, effect estimate with confidence interval, sample-size…
- ENHANCE-ITIndependent statistical analysis of Pharmacodynamic Effects of a Free-Fatty Acid Formulation of Omega-3 Pentaenoic Acid in Adults With Hypertriglyceridemia: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…
- Enhancing Self Regulation as a Strategy for Obesity Prevention in Head Start Preschoolers: Complete Statistical AnalysisIndependent statistical analysis of Enhancing Self Regulation as a Strategy for Obesity Prevention in Head Start Preschoolers: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety, based on…
- Enzastaurin in Treating Patients With Persistent or Recurrent Ovarian Epithelial Cancer or Primary Peritoneal Cancer: Complete Statistical AnalysisIndependent statistical analysis of Enzastaurin in Treating Patients With Persistent or Recurrent Ovarian Epithelial Cancer or Primary Peritoneal Cancer: primary endpoint results, effect estimate with confidence interval, sample-size planning illustration, and safety,…